KEY Publications

Watson, G., Sayles, J., Chen, C., Elliger, S., Elliger, C., Raju, N., Kurtzman, G. and Podsakoff, G., 1998. Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus. Gene Therapy 5:1642-1649

Elliger, S.S., Elliger, C.A., Aguilar, C.P., Raju, N.R. and Watson, G.L., 1999. Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector. Gene Therapy 6:1175-1178

Elliger, S.S., Elliger, C.A., Lang, C. and Watson, G.L., 2002. Enhanced secretion and uptake of β-glucuronidase improves adeno-associated viral-mediated gene therapy of mucopolysaccharidosis type VII mice. Molec. Ther. 5:617–626

Watson, G., Bastacky, J., Belichenko, P., Buddhikot, M., Jungles, S., Vellard, M., Mobley, W. C. and Kakkis, E., 2006. Intrathecal administration of AAV vectors for the treatment of lysosomal storage in the brains of MPS I mice. Gene Therapy 13:917-925